Combining a premade SMN protein with a Spinraza-like drug (targets SMN2 gene) helped patient-derived motor neurons; potential ...

The Phase 3 STEER trial enrolled more than 100 children with SMA type 2, ages 2-17, who were able to sit, but hadn't walked ...

The top 10 most-read stories published by SMA News Today in 2024 focused on symptoms, treatments, and diagnosis.

It's been a hard year for columnist Brianna Albers, but hard times make good times better. She's decided to focus on gratitude.

An algorithm that takes into account clinical measures of motor symptom severity alongside data on factors like age and height may help predict the risk of scoliosis in people with spinal muscular ...

Have you ever dreamed of being a princess (or a prince)? I think most of us have, adults included. I’ve always been a Disney fan, and it has no shortage of princesses to choose from. Each one is ...

Edward Smith, MD, is an adjunct professor of pediatrics at Duke University Hospital. He earned his medical degree from the University of Mississippi School of Medicine and has practiced since 2007. He ...

Our baby Jeffrey, who was diagnosed with SMA in July 1997, made the most of his brief earthly stint. I’ve mentioned before that our SMA duty, which lasted mere weeks between Jeffrey’s diagnosis and ...

SMA Europe is launching an initiative to share personal stories of how treatment affects the lives of people with spinal muscular atrophy (SMA). The initiative comes as part of OdySMA, an SMA Europe ...

Natalie Katz, MD, is an assistant professor of pediatrics in the division of neurology at Duke University and co-directs the Duke Children’s Neuromuscular Program, which provides comprehensive ...